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GroundBreaking New Drug For Cystic Fibrosis Released…With 1 Major Drawback

Cystic Fibrosis (CF) is one of the most devastating diseases known to mankind.

Affecting 30,000 in the U.S. alone there is no known cure for this disease.

Its particularly devastating  not just because of its ability to cripple those affected by it, but because of how long it persists and how damaging it is to the human body.

Cystic Fibrosis symptoms involves excessive mucosal build up in both the lungs and airways of those afflicted. Until recently those suffering from the disease had very little treatment options available to them. Some of the options included manual release of the mucous via manually pounding at the chest and back to loosen the mucous, or using a machine to assist with the same procedure.

But now there’s a new drug out on the market that promises to help those with CF.

A press release concerning the unveiling of the new drug sent ripples of  ecstasy through the community.

UpNorthLive reported:

According to the Cystic Fibrosis Foundation, the new drug, Orkambi, can be used for people with CF who are 12 years and older that have two copies of the F508del gene mutation, the most common CF mutation. The FDA officially announced the approval of Orkambi on July 2.

The CF Foundation says that Orkambi is a step closer to discovery and development of innovative therapies that target the root cause of CF to improve key symptoms of the disease.

“We are thrilled with the FDA’s decision,” President and CEO of the Cystic Fibrosis Foundation Robert Beall said. “The approval marks a major milestone in our decades-long effort to spur discovery and development of innovative therapies that target the root cause of CF to improve key symptoms of the disease.”

While this is exciting there is one major caveat to this announcement, one that should make anyone who’s already upset about the incredible cost of medicine sick.

The expected price tag for a year’s worth of treatment is expected to ring up at an astronomical $300,000 a year.

And treatment will be required each year and every year the affected patient is alive.

There’s no doubt the drug holds very real promise.

Jeff Masters, 37, who’s a medical sales representative, has taken Orkambi for the past two years in clinical trial said “I’m overwhelmed with joy…The impact of this drug on quality of life is very real.”

But the drug doesn’t cure CF it just works to counteracts the damage caused by the disease and helps patients to breath easier.

Considering the hefty price tag, it sure does leave a sour taste in the mouth of an exciting announcement don’t you agree?

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Category: Prescription Drugs, Wellness

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